Cell and Gene Therapy

Human Gene Therapy

The purpose of human gene therapy is to treat or prevent disease by altering genes. Methods include modifying unwanted genes, repairing damaged ones, and introducing new ones. The purpose of this technique is to address the underlying genetic causes of disorders such as haemophilia, muscular dystrophy, and cystic fibrosis. Gene therapy presents the possibility of long-term, maybe curative treatments for a variety of genetic disorders.